Liaison(s): Geoffrey Berguig, Jonathan LeBowitz
BioMarin would like to streamline the process of identifying new disease targets. To address this unmet need, the BioMarin TMP team was tasked first with developing a metabolic disease database, and second, providing preliminary recommendations on disease targets for BioMarin to pursue. The team’s goal was to identify targets that are both mission aligned and commercially viable. The team will provide detailed disease profiles and several options for therapeutic approaches. Ultimately, it is hoped that BioMarin will successfully investigate and develop treatments for one or more of these targets.