Advisory Board

The advisory board brings together representatives of each of the groups essential to the success of the Center for Rare Disease Therapies. Its members are individuals with broad expertise and wide influence in the biomedical industry, government agencies, patient organizations, and research institutions.

Blanca Aguiar, MD
Pediatrician, Private Practice

Daniel Bradbury, DMS
Managing Member, BioBrit LLC

Jonathan D. Bui, PhD Assistant Professor, Neurologist
University of California, San Diego

Tim Coté, MD, MPH
Principal, Coté Orphan Consulting

Robert Curry, PhD
Partner, Latterell Venture Partners and Chairman of the KGI Board of Trustees

Daniel Darvish, MD
Co-Founder, ARM & Founder HIBM Research Group

Diane Dorman
Vice President for Public Policy, National Organization for Rare Disorders (NORD)

Dennis M. Fenton, PhD
Principal, Fenton & Associates, LLC

Chris Garabedian
Former President & CEO Sarepta Therapeutics

Steven Groft, PharmD
Retired Director, Rare Diseases Research, National Institutes of Health (NIH)

Marlene Haffner, CEO, MD, MPH
Health Policy and Global Drug Development Consultant, Haffner Associates, LLC

Richard Haas
Professor of Neurosciences and Pediatrics, UCSD Medical Center

Peter Barton Hutt, LLB, LLM
Senior Counsel, Covington & Burling

Greg Lapointe, MBA
CEO, Cerium Pharmaceuticals

Peter Saltonstall
President and Chief Executive Officer, National Organization for Rare Disorders (NORD)

Sheldon M. Schuster, PhD
President, KGI

Barbara Wuebbels, RN, MS
Manager, Medical Affairs Investigator Relations, Biomarin Pharmaceuticals Inc.

Board of Experts

The Board of Experts for the Center for Rare Disease Therapies consists of medical experts and others whose individual knowledge of specific rare diseases can help the center increase understanding of these disorders and bring about potential therapies to treat them.

Blanca Aguiar, MD

Jon Bui, MD, PhD
Neurologist, University of California, San Diego

Daniel Darvish, MD
Co-Founder, ARM & HIBM Research Group (HRG)

Edward R.B. McCabe, MD, PhD
Physician-in-Chief, Mattel Children’s Hospital, University of California, Los Angeles

Alan Rothfeld, MD
Clinical Professor of Pulmonary and Critical Care Medicine, Keck School of Medicine, University of Southern California

Joseph Villafranca, PhD
Senior Vice President, Operations, Tunnell Consulting